TY  - GEN
TI  - Gene Therapy Briefs
SN  - 2324-8645
PY  - 2020///0303
KW  - Genetic Therapy
KW  - Humans
KW  - Muscular Atrophy, Spinal
KW  - genetics
KW  - Survival of Motor Neuron 1 Protein
KW  - United States
KW  - United States Food and Drug Administration
N1  - Publication Type: Journal Article
UR  - https://doi.org/10.1089/humc.2019.29045.bfs
ER  -