Gene Therapy Briefs. [electronic resource]
- Human gene therapy. Clinical development 06 2019
- 43-46 p. digital
Publication Type: Journal Article
2324-8645
10.1089/humc.2019.29045.bfs doi
Genetic Therapy Humans Muscular Atrophy, Spinal--genetics Survival of Motor Neuron 1 Protein--genetics United States United States Food and Drug Administration