Gene Therapy Briefs. [electronic resource] - Human gene therapy. Clinical development 06 2019 - 43-46 p. digital

Publication Type: Journal Article

2324-8645

10.1089/humc.2019.29045.bfs doi


Genetic Therapy
Humans
Muscular Atrophy, Spinal--genetics
Survival of Motor Neuron 1 Protein--genetics
United States
United States Food and Drug Administration