In vivo genome editing rescues photoreceptor degeneration via a Cas9/RecA-mediated homology-directed repair pathway. [electronic resource]
- Science advances 04 2019
- eaav3335 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
2375-2548
10.1126/sciadv.aav3335 doi
Animals CRISPR-Cas Systems--genetics Cyclic Nucleotide Phosphodiesterases, Type 6--genetics DNA Repair Electroporation Gene Editing--methods Humans Mice Mice, Inbred C57BL Rec A Recombinases--metabolism Retinal Degeneration--therapy Retinal Rod Photoreceptor Cells--metabolism RNA, Guide, CRISPR-Cas Systems