Treatment Strategies for Deficiency of Adenosine Deaminase 2. [electronic resource]
- The New England journal of medicine 04 2019
- 1582-1584 p. digital
Publication Type: Letter
1533-4406
10.1056/NEJMc1801927 doi
Adalimumab--therapeutic use Adenosine Deaminase--deficiency Adolescent Adult Antibodies, Monoclonal--therapeutic use Child Child, Preschool Drug Therapy, Combination Etanercept--therapeutic use Humans Infliximab--therapeutic use Intercellular Signaling Peptides and Proteins--deficiency Metabolism, Inborn Errors--drug therapy Plasma Secondary Prevention Stroke--prevention & control Tumor Necrosis Factor-alpha--antagonists & inhibitors Young Adult