Angelbello, Alicia J <br/><br/>
Precise small-molecule cleavage of an r(CUG) repeat expansion in a myotonic dystrophy mouse model.  [electronic resource] 

 -  Proceedings of the National Academy of Sciences of the United States of America  04 2019 
 - 7799-7804 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1091-6490 
<br/><br/><label>Standard No.: </label>10.1073/pnas.1901484116  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Bleomycin--analogs & derivatives<br/>Disease Models, Animal<br/>Drug Design<br/>Humans<br/>Mice<br/>Myotonic Dystrophy--genetics<br/>Oligonucleotides--chemistry<br/>RNA--genetics<br/>RNA Splicing--genetics<br/>Trinucleotide Repeat Expansion--genetics