Smith, Neil <br/><br/>
Phase I clinical evaluation of CNSA-001 (sepiapterin), a novel pharmacological treatment for phenylketonuria and tetrahydrobiopterin deficiencies, in healthy volunteers.  [electronic resource] 

 -  Molecular genetics and metabolism  04 2019 
 - 406-412 p.  digital 
<br/><br/> Publication Type: Clinical Trial, Phase I; Journal Article; Randomized Controlled Trial 
<br/><br/><label>ISSN: </label>1096-7206 
<br/><br/><label>Standard No.: </label>10.1016/j.ymgme.2019.02.001  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Administration, Oral<br/>Adult<br/>Australia<br/>Biopterins--analogs & derivatives<br/>Dose-Response Relationship, Drug<br/>Double-Blind Method<br/>Drug Compounding<br/>Female<br/>Healthy Volunteers<br/>Humans<br/>Male<br/>Phenylalanine<br/>Phenylketonurias--drug therapy<br/>Pterins--administration & dosage<br/>Serotonin