Fok, Wilson Chun

Posttranscriptional modulation of TERC by PAPD5 inhibition rescues hematopoietic development in dyskeratosis congenita. [electronic resource] - Blood 03 2019 - 1308-1312 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.

1528-0020

10.1182/blood-2018-11-885368 doi


Cell Cycle Proteins--genetics
Dyskeratosis Congenita--metabolism
Embryonic Stem Cells--cytology
Exosome Multienzyme Ribonuclease Complex--genetics
Hematopoiesis
Humans
Mutation
Nuclear Proteins--genetics
RNA--genetics
RNA Nucleotidyltransferases--antagonists & inhibitors
RNA Processing, Post-Transcriptional
RNA-Binding Proteins--genetics
Telomerase--genetics
Telomere