TY  - GEN
AU  - van Putten,Maaike
AU  - Tanganyika-de Winter,Christa
AU  - Bosgra,Sieto
AU  - Aartsma-Rus,Annemieke
TI  - Nonclinical Exon Skipping Studies with 2'-O-Methyl Phosphorothioate Antisense Oligonucleotides in mdx and mdx-utrn-/- Mice Inspired by Clinical Trial Results
SN  - 2159-3345
PY  - 2020///0722
KW  - Animals
KW  - Clinical Trials as Topic
KW  - Dystrophin
KW  - antagonists & inhibitors
KW  - Exons
KW  - drug effects
KW  - Genetic Therapy
KW  - Humans
KW  - Mice
KW  - Mice, Inbred mdx
KW  - Morpholinos
KW  - genetics
KW  - Muscular Atrophy, Spinal
KW  - Muscular Dystrophy, Duchenne
KW  - Oligonucleotides
KW  - pharmacology
KW  - Oligonucleotides, Antisense
KW  - Organothiophosphorus Compounds
KW  - Utrophin
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1089/nat.2018.0759
ER  -