TY  - GEN
AU  - Son,Ye Seul
AU  - Choi,Kwangman
AU  - Lee,Hana
AU  - Kwon,Ohman
AU  - Jung,Kwang Bo
AU  - Cho,Sunwha
AU  - Baek,Jiyeon
AU  - Son,Bora
AU  - Kang,Sung-Min
AU  - Kang,Mingu
AU  - Yoon,Jihee
AU  - Shen,Haihong
AU  - Lee,Sangku
AU  - Oh,Jung-Hwa
AU  - Lee,Hyang-Ae
AU  - Lee,Mi-Ok
AU  - Cho,Hyun-Soo
AU  - Jung,Cho-Rok
AU  - Kim,Janghwan
AU  - Cho,Sungchan
AU  - Son,Mi-Young
TI  - A SMN2 Splicing Modifier Rescues the Disease Phenotypes in an In Vitro Human Spinal Muscular Atrophy Model
SN  - 1557-8534
PY  - 2020///0305
KW  - Alternative Splicing
KW  - drug effects
KW  - Animals
KW  - Cell Line
KW  - Glycine
KW  - analogs & derivatives
KW  - Humans
KW  - Mice
KW  - Mice, Transgenic
KW  - Models, Neurological
KW  - Muscular Atrophy, Spinal
KW  - drug therapy
KW  - Sulfones
KW  - pharmacology
KW  - Survival of Motor Neuron 2 Protein
KW  - biosynthesis
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1089/scd.2018.0181
ER  -