Muntoni, Francesco

A Phase 1b Trial to Assess the Pharmacokinetics of Ezutromid in Pediatric Duchenne Muscular Dystrophy Patients on a Balanced Diet. [electronic resource] - Clinical pharmacology in drug development 10 2019 - 922-933 p. digital

Publication Type: Clinical Trial, Phase I; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't

2160-7648

10.1002/cpdd.642 doi


Administration, Oral
Adolescent
Benzoxazoles--administration & dosage
Child
Diet
Double-Blind Method
Drug Administration Schedule
Humans
Male
Muscular Dystrophy, Duchenne--drug therapy
Suspensions
Utrophin--antagonists & inhibitors