Przybilla, Michael J

Comprehensive behavioral and biochemical outcomes of novel murine models of GM1-gangliosidosis and Morquio syndrome type B. [electronic resource] - Molecular genetics and metabolism 02 2019 - 139-150 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1096-7206

10.1016/j.ymgme.2018.11.002 doi


Animals
CRISPR-Cas Systems
Disease Models, Animal
Female
Fluorometry
Gangliosidosis, GM1--genetics
Gene Editing
Mental Status and Dementia Tests
Mice
Mice, Inbred C57BL
Mice, Knockout
Mucopolysaccharidosis IV--genetics
Mutation
Mutation, Missense
Phenotype
beta-Galactosidase--genetics