Comprehensive behavioral and biochemical outcomes of novel murine models of GM1-gangliosidosis and Morquio syndrome type B. [electronic resource]
- Molecular genetics and metabolism 02 2019
- 139-150 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1096-7206
10.1016/j.ymgme.2018.11.002 doi
Animals CRISPR-Cas Systems Disease Models, Animal Female Fluorometry Gangliosidosis, GM1--genetics Gene Editing Mental Status and Dementia Tests Mice Mice, Inbred C57BL Mice, Knockout Mucopolysaccharidosis IV--genetics Mutation Mutation, Missense Phenotype beta-Galactosidase--genetics