Braunlin, Elizabeth

Hematopoietic cell transplantation for severe MPS I in the first six months of life: The heart of the matter. [electronic resource] - Molecular genetics and metabolism 02 2019 - 117-120 p. digital

Publication Type: Journal Article

1096-7206

10.1016/j.ymgme.2018.11.007 doi


Enzyme Replacement Therapy
Female
Heart--physiopathology
Hematopoietic Stem Cell Transplantation
Humans
Infant
Infant, Newborn
Male
Mucopolysaccharidosis I--diagnosis
Neonatal Screening