Tamò, Raphaël

[The basics of lysosomal storage diseases]. [electronic resource] - Therapeutische Umschau. Revue therapeutique Nov 2018 - 199-207 p. digital

Publication Type: Journal Article

0040-5930

10.1024/0040-5930/a000990 doi


Enzyme Replacement Therapy
Genetic Therapy
Hematopoietic Stem Cell Transplantation
Humans
Lysosomal Storage Diseases
Lysosomes