Tamò, Raphaël
[The basics of lysosomal storage diseases]. [electronic resource]
- Therapeutische Umschau. Revue therapeutique Nov 2018
- 199-207 p. digital
Publication Type: Journal Article
0040-5930
10.1024/0040-5930/a000990 doi
Enzyme Replacement Therapy
Genetic Therapy
Hematopoietic Stem Cell Transplantation
Humans
Lysosomal Storage Diseases
Lysosomes