Wang, Yanchi

Paired CRISPR/Cas9 Nickases Mediate Efficient Site-Specific Integration of [electronic resource] - International journal of molecular sciences Oct 2018

Publication Type: Journal Article

1422-0067

10.3390/ijms19103035 doi


Animals
CRISPR-Associated Protein 9--genetics
Clustered Regularly Interspaced Short Palindromic Repeats--genetics
DNA, Ribosomal--genetics
Deoxyribonuclease I--genetics
Factor IX--genetics
Gene Targeting--methods
Genetic Loci
Hemophilia B--therapy
Hepatocytes--cytology
Humans
Mice
Mice, SCID
Mouse Embryonic Stem Cells--cytology