TY - GEN AU - Barthélémy,Florian AU - Courrier,Sébastien AU - Lévy,Nicolas AU - Krahn,Martin AU - Bartoli,Marc TI - Dysferlin Exon 32 Skipping in Patient Cells SN - 1940-6029 PY - 2019///0401 KW - Cell Differentiation KW - genetics KW - Cells, Cultured KW - Dysferlin KW - Exons KW - Gene Expression Regulation KW - Humans KW - Muscular Dystrophies KW - Myoblasts KW - cytology KW - Oligonucleotides, Antisense KW - administration & dosage KW - RNA Editing KW - RNA Splicing N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.1007/978-1-4939-8651-4_31 ER -