Barthélémy, Florian

Dysferlin Exon 32 Skipping in Patient Cells. [electronic resource] - Methods in molecular biology (Clifton, N.J.) 2018 - 489-496 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1940-6029

10.1007/978-1-4939-8651-4_31 doi


Cell Differentiation--genetics
Cells, Cultured
Dysferlin--genetics
Exons
Gene Expression Regulation
Humans
Muscular Dystrophies--genetics
Myoblasts--cytology
Oligonucleotides, Antisense--administration & dosage
RNA Editing
RNA Splicing