Röth, Alexander

Ravulizumab (ALXN1210) in patients with paroxysmal nocturnal hemoglobinuria: results of 2 phase 1b/2 studies. [electronic resource] - Blood advances 09 2018 - 2176-2185 p. digital

Publication Type: Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't

2473-9537

10.1182/bloodadvances.2018020644 doi


Adult
Antibodies, Monoclonal, Humanized--administration & dosage
Complement C5--antagonists & inhibitors
Female
Hemoglobinuria, Paroxysmal--drug therapy
Hemolysis--drug effects
Humans
L-Lactate Dehydrogenase--blood
Male
Middle Aged
Quality of Life
Treatment Outcome