TY  - GEN
AU  - Cideciyan,Artur V
AU  - Sudharsan,Raghavi
AU  - Dufour,Valérie L
AU  - Massengill,Michael T
AU  - Iwabe,Simone
AU  - Swider,Malgorzata
AU  - Lisi,Brianna
AU  - Sumaroka,Alexander
AU  - Marinho,Luis Felipe
AU  - Appelbaum,Tatyana
AU  - Rossmiller,Brian
AU  - Hauswirth,William W
AU  - Jacobson,Samuel G
AU  - Lewin,Alfred S
AU  - Aguirre,Gustavo D
AU  - Beltran,William A
TI  - Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector
SN  - 1091-6490
PY  - 2018///1005
KW  - Animals
KW  - Dependovirus
KW  - Dogs
KW  - Gene Knock-In Techniques
KW  - methods
KW  - Gene Knockdown Techniques
KW  - Genetic Therapy
KW  - Genetic Vectors
KW  - HEK293 Cells
KW  - Humans
KW  - RNA, Catalytic
KW  - biosynthesis
KW  - Retinal Rod Photoreceptor Cells
KW  - metabolism
KW  - Retinitis Pigmentosa
KW  - genetics
KW  - Rhodopsin
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1073/pnas.1805055115
ER  -