Tingley, Kylie <br/><br/>
Using a meta-narrative literature review and focus groups with key stakeholders to identify perceived challenges and solutions for generating robust evidence on the effectiveness of treatments for rare diseases.  [electronic resource] 

 -  Orphanet journal of rare diseases  06 2018 
 - 104 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review 
<br/><br/><label>ISSN: </label>1750-1172 
<br/><br/><label>Standard No.: </label>10.1186/s13023-018-0851-1  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Focus Groups<br/>Humans<br/>Rare Diseases<br/>Research Design