TY  - GEN
AU  - Keeler,Allison M
AU  - Zieger,Marina
AU  - Todeasa,Sophia H
AU  - McCall,Angela L
AU  - Gifford,Jennifer C
AU  - Birsak,Samantha
AU  - Choudhury,Sourav R
AU  - Byrne,Barry J
AU  - Sena-Esteves,Miguel
AU  - ElMallah,Mai K
TI  - Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease
SN  - 1557-7422
PY  - 2020///0311
KW  - Animals
KW  - Dependovirus
KW  - genetics
KW  - Disease Models, Animal
KW  - Enzyme Activation
KW  - Gene Expression
KW  - Gene Transfer Techniques
KW  - Genetic Therapy
KW  - methods
KW  - Genetic Vectors
KW  - administration & dosage
KW  - Glycogen
KW  - metabolism
KW  - Glycogen Storage Disease Type II
KW  - Humans
KW  - Immunohistochemistry
KW  - Mice
KW  - Mice, Transgenic
KW  - Muscle, Skeletal
KW  - Prognosis
KW  - Treatment Outcome
KW  - alpha-Glucosidases
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1089/hum.2018.016
ER  -