TY - GEN AU - Kuo,Caroline Y AU - Long,Joseph D AU - Campo-Fernandez,Beatriz AU - de Oliveira,Satiro AU - Cooper,Aaron R AU - Romero,Zulema AU - Hoban,Megan D AU - Joglekar,Alok V AU - Lill,Georgia R AU - Kaufman,Michael L AU - Fitz-Gibbon,Sorel AU - Wang,Xiaoyan AU - Hollis,Roger P AU - Kohn,Donald B TI - Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome SN - 2211-1247 PY - 2019///1105 KW - Animals KW - Antigens, CD34 KW - metabolism KW - Base Sequence KW - CD40 Ligand KW - CRISPR-Associated Protein 9 KW - CRISPR-Cas Systems KW - genetics KW - Cell Differentiation KW - Cell Line KW - Colony-Forming Units Assay KW - DNA Repair KW - DNA, Complementary KW - Gene Editing KW - Genetic Diseases, X-Linked KW - Hematopoietic Stem Cells KW - Humans KW - Hyper-IgM Immunodeficiency Syndrome KW - Mice KW - T-Lymphocytes KW - Transcription Activator-Like Effector Nucleases N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.1016/j.celrep.2018.04.103 ER -