Kuo, Caroline Y <br/><br/>
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome.  [electronic resource] 

 -  Cell reports  05 2018 
 - 2606-2616 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>2211-1247 
<br/><br/><label>Standard No.: </label>10.1016/j.celrep.2018.04.103  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Antigens, CD34--metabolism<br/>Base Sequence<br/>CD40 Ligand--metabolism<br/>CRISPR-Associated Protein 9--metabolism<br/>CRISPR-Cas Systems--genetics<br/>Cell Differentiation<br/>Cell Line<br/>Colony-Forming Units Assay<br/>DNA Repair<br/>DNA, Complementary--genetics<br/>Gene Editing<br/>Genetic Diseases, X-Linked--genetics<br/>Hematopoietic Stem Cells--metabolism<br/>Humans<br/>Hyper-IgM Immunodeficiency Syndrome--genetics<br/>Mice<br/>T-Lymphocytes--metabolism<br/>Transcription Activator-Like Effector Nucleases--metabolism