Lim, Jeong-A <br/><br/>
Therapeutic Benefit of Autophagy Modulation in Pompe Disease.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  07 2018 
 - 1783-1796 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1016/j.ymthe.2018.04.025  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Autophagy--physiology<br/>Disease Models, Animal<br/>Enzyme Replacement Therapy--methods<br/>Female<br/>Glycogen--metabolism<br/>Glycogen Storage Disease Type II--metabolism<br/>Lysosomes--metabolism<br/>Male<br/>Mice<br/>Mice, Knockout<br/>Muscle, Skeletal--metabolism<br/>TOR Serine-Threonine Kinases--metabolism<br/>Up-Regulation--physiology<br/>alpha-Glucosidases--metabolism