TY  - GEN
AU  - Spada,Marco
AU  - Baron,Ralf
AU  - Elliott,Perry M
AU  - Falissard,Bruno
AU  - Hilz,Max J
AU  - Monserrat,Lorenzo
AU  - Tøndel,Camilla
AU  - Tylki-Szymańska,Anna
AU  - Wanner,Christoph
AU  - Germain,Dominique P
TI  - The effect of enzyme replacement therapy on clinical outcomes in paediatric patients with Fabry disease - A systematic literature review by a European panel of experts
SN  - 1096-7206
PY  - 2019///1104
KW  - Child
KW  - Enzyme Replacement Therapy
KW  - Europe
KW  - Fabry Disease
KW  - therapy
KW  - Female
KW  - Humans
KW  - Isoenzymes
KW  - therapeutic use
KW  - Male
KW  - Observational Studies as Topic
KW  - Pain
KW  - drug therapy
KW  - Quality of Life
KW  - Randomized Controlled Trials as Topic
KW  - Recombinant Proteins
KW  - Treatment Outcome
KW  - Trihexosylceramides
KW  - metabolism
KW  - alpha-Galactosidase
N1  - Publication Type: Journal Article; Systematic Review
UR  - https://doi.org/10.1016/j.ymgme.2018.04.007
ER  -