TY  - GEN
AU  - Schneider,Raphael
TI  - CIM Journal Club: Gene therapy for spinal muscular atrophy Comment on Mendell et al. N Engl J Med 2017;377:1713-22
SN  - 1488-2353
PY  - 2018///1225
KW  - Child
KW  - Genetic Therapy
KW  - Humans
KW  - Infant
KW  - Muscular Atrophy, Spinal
KW  - Survival of Motor Neuron 1 Protein
KW  - genetics
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Comment
UR  - https://doi.org/10.25011/cim.v41i1.29461
ER  -