TY  - GEN
AU  - Prieve,Mary G
AU  - Harvie,Pierrot
AU  - Monahan,Sean D
AU  - Roy,Debashish
AU  - Li,Allen G
AU  - Blevins,Teri L
AU  - Paschal,Amber E
AU  - Waldheim,Matt
AU  - Bell,Eric C
AU  - Galperin,Anna
AU  - Ella-Menye,Jean-Rene
AU  - Houston,Michael E
TI  - Targeted mRNA Therapy for Ornithine Transcarbamylase Deficiency
SN  - 1525-0024
PY  - 2019///0315
KW  - Animals
KW  - Disease Models, Animal
KW  - Genetic Therapy
KW  - methods
KW  - Male
KW  - Metabolic Networks and Pathways
KW  - Mice
KW  - Mice, Knockout
KW  - Micelles
KW  - Nanoparticles
KW  - Nanotechnology
KW  - Ornithine Carbamoyltransferase
KW  - genetics
KW  - Ornithine Carbamoyltransferase Deficiency Disease
KW  - Polymers
KW  - RNA, Messenger
KW  - administration & dosage
KW  - RNA, Small Interfering
KW  - Urea
KW  - metabolism
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1016/j.ymthe.2017.12.024
ER  -