Hinderer, Christian <br/><br/>
Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.  [electronic resource] 

 -  Human gene therapy  03 2018 
 - 285-298 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1557-7422 
<br/><br/><label>Standard No.: </label>10.1089/hum.2018.015  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Dependovirus<br/>Ganglia, Spinal--metabolism<br/>Genetic Vectors--adverse effects<br/>Haplorhini<br/>Humans<br/>Sensory Receptor Cells--metabolism<br/>Survival of Motor Neuron 1 Protein--biosynthesis<br/>Swine<br/>Time Factors<br/>Transaminases--blood<br/>Transgenes