McClements, Michelle E Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes. [electronic resource] - The Yale journal of biology and medicine 12 2017 - 611-623 p. digital Publication Type: Journal Article; Review ISSN: 1551-4056 Subjects--Topical Terms: AnimalsDNA, Single-StrandedDependovirus--geneticsGenetic Therapy--methodsGenetic VectorsHumansRetinal Degeneration--geneticsTerminal Repeat SequencesTransgenes