McClements, Michelle E

Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes. [electronic resource] - The Yale journal of biology and medicine 12 2017 - 611-623 p. digital

Publication Type: Journal Article; Review

1551-4056


Animals
DNA, Single-Stranded
Dependovirus--genetics
Genetic Therapy--methods
Genetic Vectors
Humans
Retinal Degeneration--genetics
Terminal Repeat Sequences
Transgenes