Binding to SMN2 pre-mRNA-protein complex elicits specificity for small molecule splicing modifiers. [electronic resource]
- Nature communications 11 2017
- 1476 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
2041-1723
10.1038/s41467-017-01559-4 doi
Biflavonoids--pharmacology Cell-Free System Computational Biology Epoxy Compounds--pharmacology Exons--genetics Fibroblasts HEK293 Cells HeLa Cells Humans Ligands Macrolides--pharmacology Muscular Atrophy, Spinal--drug therapy Piperazines--chemical synthesis Protein Binding Protein Structure, Quaternary Proteomics--methods RNA Precursors--genetics RNA Splicing--drug effects RNA, Messenger--genetics RNA-Binding Proteins--metabolism Spliceosomes--drug effects Survival of Motor Neuron 1 Protein--genetics Survival of Motor Neuron 2 Protein--genetics