TY - GEN AU - Kuperus,Esther AU - Kruijshaar,Michelle E AU - Wens,Stephan C A AU - de Vries,Juna M AU - Favejee,Marein M AU - van der Meijden,Jan C AU - Rizopoulos,Dimitris AU - Brusse,Esther AU - van Doorn,Pieter A AU - van der Ploeg,Ans T AU - van der Beek,Nadine A M E TI - Long-term benefit of enzyme replacement therapy in Pompe disease: A 5-year prospective study SN - 1526-632X PY - 2017///1212 KW - Activities of Daily Living KW - Adult KW - Aged KW - Cohort Studies KW - Enzyme Replacement Therapy KW - adverse effects KW - Female KW - Follow-Up Studies KW - Glycogen Storage Disease Type II KW - drug therapy KW - Humans KW - Male KW - Middle Aged KW - Muscle Strength KW - Muscle Strength Dynamometer KW - Prospective Studies KW - Respiratory Function Tests KW - Treatment Outcome KW - Walk Test KW - Young Adult KW - alpha-Glucosidases KW - therapeutic use N1 - Publication Type: Journal Article UR - https://doi.org/10.1212/WNL.0000000000004711 ER -