Kuperus, Esther <br/><br/>
Long-term benefit of enzyme replacement therapy in Pompe disease: A 5-year prospective study.  [electronic resource] 

 -  Neurology  Dec 2017 
 - 2365-2373 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>1526-632X 
<br/><br/><label>Standard No.: </label>10.1212/WNL.0000000000004711  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Activities of Daily Living<br/>Adult<br/>Aged<br/>Cohort Studies<br/>Enzyme Replacement Therapy--adverse effects<br/>Female<br/>Follow-Up Studies<br/>Glycogen Storage Disease Type II--drug therapy<br/>Humans<br/>Male<br/>Middle Aged<br/>Muscle Strength<br/>Muscle Strength Dynamometer<br/>Prospective Studies<br/>Respiratory Function Tests<br/>Treatment Outcome<br/>Walk Test<br/>Young Adult<br/>alpha-Glucosidases--therapeutic use