TY  - GEN
AU  - Wood,Matthew J A
AU  - Talbot,Kevin
AU  - Bowerman,Melissa
TI  - Spinal muscular atrophy: antisense oligonucleotide therapy opens the door to an integrated therapeutic landscape
SN  - 1460-2083
PY  - 2018///0305
KW  - Animals
KW  - Central Nervous System
KW  - metabolism
KW  - Disease Models, Animal
KW  - Exons
KW  - Humans
KW  - Mice
KW  - Motor Neurons
KW  - Muscular Atrophy, Spinal
KW  - genetics
KW  - Oligodeoxyribonucleotides, Antisense
KW  - Oligonucleotides
KW  - therapeutic use
KW  - Oligonucleotides, Antisense
KW  - administration & dosage
KW  - RNA, Messenger
KW  - Spinal Cord
KW  - Survival of Motor Neuron 1 Protein
KW  - Survival of Motor Neuron 2 Protein
N1  - Publication Type: Journal Article; Review
UR  - https://doi.org/10.1093/hmg/ddx215
ER  -