Wood, Matthew J A <br/><br/>
Spinal muscular atrophy: antisense oligonucleotide therapy opens the door to an integrated therapeutic landscape.  [electronic resource] 

 -  Human molecular genetics  10 2017 
 - R151-R159 p.  digital 
<br/><br/> Publication Type: Journal Article; Review 
<br/><br/><label>ISSN: </label>1460-2083 
<br/><br/><label>Standard No.: </label>10.1093/hmg/ddx215  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Central Nervous System--metabolism<br/>Disease Models, Animal<br/>Exons<br/>Humans<br/>Mice<br/>Motor Neurons--metabolism<br/>Muscular Atrophy, Spinal--genetics<br/>Oligodeoxyribonucleotides, Antisense--genetics<br/>Oligonucleotides--therapeutic use<br/>Oligonucleotides, Antisense--administration & dosage<br/>RNA, Messenger--genetics<br/>Spinal Cord--metabolism<br/>Survival of Motor Neuron 1 Protein--genetics<br/>Survival of Motor Neuron 2 Protein--genetics