TY  - GEN
AU  - Hashem,Hasan
AU  - Kumar,Ashish R
AU  - Müller,Ingo
AU  - Babor,Florian
AU  - Bredius,Robbert
AU  - Dalal,Jignesh
AU  - Hsu,Amy P
AU  - Holland,Steven M
AU  - Hickstein,Dennis D
AU  - Jolles,Stephen
AU  - Krance,Robert
AU  - Sasa,Ghadir
AU  - Taskinen,Mervi
AU  - Koskenvuo,Minna
AU  - Saarela,Janna
AU  - van Montfrans,Joris
AU  - Wilson,Keith
AU  - Bosch,Barbara
AU  - Moens,Leen
AU  - Hershfield,Michael
AU  - Meyts,Isabelle
TI  - Hematopoietic stem cell transplantation rescues the hematological, immunological, and vascular phenotype in DADA2
SN  - 1528-0020
PY  - 2017///1227
KW  - Adenosine Deaminase
KW  - blood
KW  - Adolescent
KW  - Child
KW  - Child, Preschool
KW  - Cohort Studies
KW  - Female
KW  - Graft vs Host Disease
KW  - diagnosis
KW  - Hematopoietic Stem Cell Transplantation
KW  - adverse effects
KW  - Humans
KW  - Immunologic Deficiency Syndromes
KW  - enzymology
KW  - Infant
KW  - Infant, Newborn
KW  - Intercellular Signaling Peptides and Proteins
KW  - Male
KW  - Mutation
KW  - Phenotype
KW  - Transplantation Conditioning
KW  - methods
N1  - Publication Type: Journal Article; Multicenter Study
UR  - https://doi.org/10.1182/blood-2017-07-798660
ER  -