Franco, José Francisco da Silva Mucopolysaccharidosis type I, II and VI and response to enzyme replacement therapy: Results from a single-center case series study. [electronic resource] - Intractable & rare diseases research Aug 2017 - 183-190 p. digital Publication Type: Journal Article ISSN: 2186-3644 Standard No.: 10.5582/irdr.2017.01036 doi