Chiriboga, Claudia A
Nusinersen for the treatment of spinal muscular atrophy. [electronic resource]
- Expert review of neurotherapeutics Oct 2017
- 955-962 p. digital
Publication Type: Journal Article; Review
1744-8360
10.1080/14737175.2017.1364159 doi
Adolescent
Child
Child, Preschool
Humans
Infant
Muscular Atrophy, Spinal--drug therapy
Oligonucleotides--pharmacology
Oligonucleotides, Antisense--pharmacology