Wanner, Adam Clinical Trial Design for Alpha-1 Antitrypsin Deficiency: A Model for Rare Diseases. [electronic resource] - Chronic obstructive pulmonary diseases (Miami, Fla.) Apr 2015 - 177-190 p. digital Publication Type: Journal Article ISSN: 2372-952X Standard No.: 10.15326/jcopdf.2.2.2015.0132 doi