TY  - GEN
AU  - Potter,Rachael A
AU  - Griffin,Danielle A
AU  - Sondergaard,Patricia C
AU  - Johnson,Ryan W
AU  - Pozsgai,Eric R
AU  - Heller,Kristin N
AU  - Peterson,Ellyn L
AU  - Lehtimäki,Kimmo K
AU  - Windish,Hillarie P
AU  - Mittal,Plavi J
AU  - Albrecht,Douglas E
AU  - Mendell,Jerry R
AU  - Rodino-Klapac,Louise R
TI  - Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy
SN  - 1557-7422
PY  - 2019///0624
KW  - Animals
KW  - DNA, Complementary
KW  - administration & dosage
KW  - Dependovirus
KW  - genetics
KW  - Disease Models, Animal
KW  - Dysferlin
KW  - Gene Expression Regulation
KW  - Genetic Therapy
KW  - Genetic Vectors
KW  - therapeutic use
KW  - Humans
KW  - Male
KW  - Mice
KW  - Muscle, Skeletal
KW  - Muscular Dystrophies, Limb-Girdle
KW  - Mutation
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1089/hum.2017.062
ER  -