Potter, Rachael A <br/><br/>
Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy.  [electronic resource] 

 -  Human gene therapy  07 2018 
 - 749-762 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1557-7422 
<br/><br/><label>Standard No.: </label>10.1089/hum.2017.062  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>DNA, Complementary--administration & dosage<br/>Dependovirus--genetics<br/>Disease Models, Animal<br/>Dysferlin--administration & dosage<br/>Gene Expression Regulation<br/>Genetic Therapy<br/>Genetic Vectors--therapeutic use<br/>Humans<br/>Male<br/>Mice<br/>Muscle, Skeletal<br/>Muscular Dystrophies, Limb-Girdle--genetics<br/>Mutation