Vijayakumar, Sarath

Rescue of peripheral vestibular function in Usher syndrome mice using a splice-switching antisense oligonucleotide. [electronic resource] - Human molecular genetics 09 2017 - 3482-3494 p. digital

Publication Type: Journal Article

1460-2083

10.1093/hmg/ddx234 doi


Animals
Carrier Proteins--genetics
Cell Cycle Proteins
Cytoskeletal Proteins
Disease Models, Animal
Evoked Potentials, Auditory
Hearing--genetics
Mice
Mutation
Oligonucleotides, Antisense--therapeutic use
Retina--metabolism
Retinal Degeneration--genetics
Usher Syndromes--genetics
Vestibular Evoked Myogenic Potentials--genetics
Vestibule, Labyrinth--metabolism