TY  - GEN
AU  - Beltran,William A
AU  - Cideciyan,Artur V
AU  - Boye,Shannon E
AU  - Ye,Guo-Jie
AU  - Iwabe,Simone
AU  - Dufour,Valerie L
AU  - Marinho,Luis Felipe
AU  - Swider,Malgorzata
AU  - Kosyk,Mychajlo S
AU  - Sha,Jin
AU  - Boye,Sanford L
AU  - Peterson,James J
AU  - Witherspoon,C Douglas
AU  - Alexander,John J
AU  - Ying,Gui-Shuang
AU  - Shearman,Mark S
AU  - Chulay,Jeffrey D
AU  - Hauswirth,William W
AU  - Gamlin,Paul D
AU  - Jacobson,Samuel G
AU  - Aguirre,Gustavo D
TI  - Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations
SN  - 1525-0024
PY  - 2018///0423
KW  - Animals
KW  - Carrier Proteins
KW  - genetics
KW  - Dependovirus
KW  - Disease Models, Animal
KW  - Dogs
KW  - Eye Proteins
KW  - G-Protein-Coupled Receptor Kinase 1
KW  - Gene Expression
KW  - Gene Order
KW  - Genes, Reporter
KW  - Genes, X-Linked
KW  - Genetic Therapy
KW  - Genetic Vectors
KW  - Humans
KW  - Mutation
KW  - Phenotype
KW  - Photoreceptor Cells, Vertebrate
KW  - metabolism
KW  - Primates
KW  - Promoter Regions, Genetic
KW  - Retina
KW  - Retinitis Pigmentosa
KW  - diagnosis
KW  - Transduction, Genetic
KW  - Transgenes
KW  - Vision Tests
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural
UR  - https://doi.org/10.1016/j.ymthe.2017.05.004
ER  -