Beltran, William A <br/><br/>
Optimization of Retinal Gene Therapy for X-Linked Retinitis Pigmentosa Due to RPGR Mutations.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  08 2017 
 - 1866-1880 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1016/j.ymthe.2017.05.004  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Carrier Proteins--genetics<br/>Dependovirus--genetics<br/>Disease Models, Animal<br/>Dogs<br/>Eye Proteins--genetics<br/>G-Protein-Coupled Receptor Kinase 1--genetics<br/>Gene Expression<br/>Gene Order<br/>Genes, Reporter<br/>Genes, X-Linked<br/>Genetic Therapy<br/>Genetic Vectors--genetics<br/>Humans<br/>Mutation<br/>Phenotype<br/>Photoreceptor Cells, Vertebrate--metabolism<br/>Primates<br/>Promoter Regions, Genetic<br/>Retina--metabolism<br/>Retinitis Pigmentosa--diagnosis<br/>Transduction, Genetic<br/>Transgenes<br/>Vision Tests