Gadalla, Kamal K E <br/><br/>
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome.  [electronic resource] 

 -  Molecular therapy. Methods & clinical development  Jun 2017 
 - 180-190 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>2329-0501 
<br/><br/><label>Standard No.: </label>10.1016/j.omtm.2017.04.007  doi