TY  - GEN
AU  - Aartsma-Rus,Annemieke
TI  - FDA Approval of Nusinersen for Spinal Muscular Atrophy Makes 2016 the Year of Splice Modulating Oligonucleotides
SN  - 2159-3345
PY  - 2018///0801
KW  - Adolescent
KW  - Adult
KW  - Alternative Splicing
KW  - drug effects
KW  - Animals
KW  - Child
KW  - Child, Preschool
KW  - Drug Approval
KW  - Humans
KW  - Infant
KW  - Models, Animal
KW  - Morpholinos
KW  - therapeutic use
KW  - Muscular Atrophy, Spinal
KW  - drug therapy
KW  - Oligonucleotides
KW  - economics
KW  - Oligonucleotides, Antisense
KW  - Survival of Motor Neuron 1 Protein
KW  - genetics
KW  - Survival of Motor Neuron 2 Protein
KW  - United States
KW  - United States Food and Drug Administration
N1  - Publication Type: Journal Article
UR  - https://doi.org/10.1089/nat.2017.0665
ER  -