Ortolano, Rita

Letter to the Editors: Concerning "Divergent clinical outcomes of alphaglucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state" by Takashi M et al. [electronic resource] - Molecular genetics and metabolism reports Jun 2017 - 1 p. digital

Publication Type: Journal Article

2214-4269

10.1016/j.ymgmr.2017.02.003 doi