TY - GEN AU - Thorne,Barb AU - Takeya,Ryan AU - Vitelli,Francesca AU - Swanson,Xin TI - Gene Therapy SN - 0724-6145 PY - 2019///0506 KW - Biopharmaceutics KW - methods KW - Genetic Therapy KW - Genetic Vectors KW - Humans N1 - Publication Type: Journal Article; Review UR - https://doi.org/10.1007/10_2016_53 ER -