Williams, Corey L

Gene Therapeutic Reversal of Peripheral Olfactory Impairment in Bardet-Biedl Syndrome. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy 04 2017 - 904-916 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural

1525-0024

10.1016/j.ymthe.2017.02.006 doi


Alleles
Animals
Bardet-Biedl Syndrome--genetics
Cilia--metabolism
Dependovirus--genetics
Disease Models, Animal
Ectopic Gene Expression
Gene Expression
Gene Transfer Techniques
Genetic Therapy
Genetic Vectors--administration & dosage
Humans
Mice
Mice, Knockout
Microtubule-Associated Proteins--genetics
Mutation
Olfactory Perception--genetics
Olfactory Receptor Neurons--metabolism
Phenotype
Protein Transport
Transduction, Genetic