Carmona, Vitor <br/><br/>
Unravelling Endogenous MicroRNA System Dysfunction as a New Pathophysiological Mechanism in Machado-Joseph Disease.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  04 2017 
 - 1038-1055 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1016/j.ymthe.2017.01.021  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>3' Untranslated Regions<br/>Animals<br/>Ataxin-3--genetics<br/>Cell Line<br/>Disease Models, Animal<br/>Gene Expression<br/>Gene Expression Regulation<br/>Gene Order<br/>Genes, Reporter<br/>Genetic Vectors--genetics<br/>Humans<br/>Lentivirus--genetics<br/>Machado-Joseph Disease--genetics<br/>Mice<br/>Mice, Transgenic<br/>MicroRNAs--genetics<br/>Mutation<br/>Neurons--metabolism<br/>Protein Aggregation, Pathological<br/>RNA Interference<br/>RNA Stability