Doulatov, Sergei

Drug discovery for Diamond-Blackfan anemia using reprogrammed hematopoietic progenitors. [electronic resource] - Science translational medicine 02 2017

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, N.I.H., Intramural; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, Non-U.S. Gov't

1946-6242

10.1126/scitranslmed.aah5645 doi


Allyl Compounds--pharmacology
Anemia, Diamond-Blackfan--drug therapy
Antigens, CD34--metabolism
Autophagy--drug effects
Autophagy-Related Protein 5--metabolism
Cell Differentiation--drug effects
Cellular Reprogramming
Drug Discovery
Erythroid Cells--drug effects
Erythropoiesis--drug effects
Genetic Complementation Test
Globins--metabolism
Hematopoietic Stem Cell Transplantation
Hematopoietic Stem Cells--drug effects
Humans
Induced Pluripotent Stem Cells--drug effects
Quinazolines--pharmacology