Shabanpoor, Fazel <br/><br/>
Identification of a Peptide for Systemic Brain Delivery of a Morpholino Oligonucleotide in Mouse Models of Spinal Muscular Atrophy.  [electronic resource] 

 -  Nucleic acid therapeutics  Jun 2017 
 - 130-143 p.  digital 
<br/><br/> Publication Type: Journal Article 
<br/><br/><label>ISSN: </label>2159-3345 
<br/><br/><label>Standard No.: </label>10.1089/nat.2016.0652  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Animals, Newborn<br/>Apolipoproteins E--chemical synthesis<br/>Biomarkers--blood<br/>Blood-Brain Barrier--chemistry<br/>Brain--cytology<br/>Cell Survival--drug effects<br/>Disease Models, Animal<br/>Exons<br/>Fibroblasts--drug effects<br/>Hepatocytes--drug effects<br/>Humans<br/>Kidney--chemistry<br/>Mice<br/>Morpholinos--chemistry<br/>Muscular Atrophy, Spinal--drug therapy<br/>Nanoconjugates--analysis<br/>Peptides--chemical synthesis<br/>Phenotype<br/>Quadriceps Muscle--chemistry<br/>Survival of Motor Neuron 2 Protein--drug effects